Examples include Exondys 51 (eteplirsen ... What foods should you avoid with muscular dystrophy? People with muscular ...

An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

Javed Shaikh, Director of RWE & HEOR, Axtria, explains how harnessing next-generation sequencing and AI-powered analytics ...

Considering taking supplements to treat muscular dystrophy? Below is a list of common natural remedies used to treat or reduce the symptoms of muscular dystrophy. Follow the links to read common ...

All fetuses affected with disease genes were born. Then, in the case of DMD, for example, if the affected child was a boy, he would mostly likely either die before reproducing or be incapable of ...

The mum of an 11-year-old boy who is waiting to find out if he can access a new drug to treat his Duchenne muscular dystrophy (DMD) said her son talked about his fear of death. Harry, from Corby ...

A patient has died following treatment with Elevidys, the Sarepta Therapeutics product that is the only FDA-approved gene therapy for Duchenne muscular dystrophy, the company disclosed Tuesday.

About Duchenne Muscular Dystrophy DMD is a progressive neuromuscular disorder caused by a mutation in the DMD gene which affects the production of a protein called dystrophin. 3 Dystrophin is a ...

Opens in a new tab or window Share on LinkedIn. Opens in a new tab or window A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...