Examples include Exondys 51 (eteplirsen ... What foods should you avoid with muscular dystrophy? People with muscular dystrophy should avoid foods high in fats and sugars. Is Duchenne always ...

Becker muscular dystrophy (BMD) is a type of muscular dystrophy, a genetic condition that weakens and damages muscles. It can worsen with age. However, its symptoms are less severe than those of ...

Two dose levels of a single-administration gene therapy were well-tolerated and led to functional improvements in ambulatory ...

neuromuscular disease or muscular dystrophy patients have. "We have also made some improvements in terms of monitoring disease, including different imaging techniques of muscles. For example, we ...

such as FSHD [facioscapulohumeral muscular dystrophy]. The goal of the gene therapy is to reduce the expression of a given protein, or pathogenic protein, and there are a variety of examples [of ...

WASHINGTON (AP) — Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for muscular dystrophy, sending company shares plummeting more than 25%.

Opens in a new tab or window Share on LinkedIn. Opens in a new tab or window A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...