Global Duchenne Muscular Dystrophy Drugs Market value attained USD 3.9 Billion in 2025. The market will achieve USD 6.5 ...

such as FSHD [facioscapulohumeral muscular dystrophy]. The goal of the gene therapy is to reduce the expression of a given protein, or pathogenic protein, and there are a variety of examples [of ...

Javed Shaikh, Director of RWE & HEOR, Axtria, explains how harnessing next-generation sequencing and AI-powered analytics ...

Discover how an emerging technology called tRNA therapy could become the next big thing in genetic disease treatment.

Euphoria and Grey's Anatomy's Eric Dane has announced he's been diagnosed with amyotrophic lateral sclerosis (ALS).

Edgewise Therapeutics shares are trading lower by 25.7% during Wednesday's session. The company announced an approximate $200 million offering.

Marks’ resignation leaves the field without a regulator many view as “integral” to its progress over the last decade.

The Trump administration's proposal to cut National Institutes of Health (NIH) indirect funds has been widely attacked, with ...

Florida leaders can enact a new law, the Right to Try for Individualized Treatments, that allows Floridians with rare ...

ITV News has uncovered further allegations of neglect of disabled adults at Lifeways and at least one council has paused new referrals. | ITV National News ...

Trial achieved key objectives for safety, tolerability, pharmacokinetics and pharmacodynamicsClinical data from this trial, together with ...

The bill advanced after testimony from the mother of a Morris County student with muscular dystrophy who died on his ride home in 2023.