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Newborn screening is also cost-effective. Testing that takes just a few dollars per baby can save families and the health ...
Examples include Exondys 51 (eteplirsen ... What foods should you avoid with muscular dystrophy? People with muscular dystrophy should avoid foods high in fats and sugars. Is Duchenne always ...
Learning life skills to handle Duchenne muscular dystrophy can include health management, working with caregivers, and ...
Two dose levels of a single-administration gene therapy were well-tolerated and led to functional improvements in ambulatory ...
A trial found magnetic resonance imaging correlated with physical function tests in patients with Duchenne muscular dystrophy ...
A major trial of a promising gene therapy for Duchenne muscular dystrophy has fallen short, but researchers say the lessons learned could pave the way for better, more effective treatments.
You can reach Jason on Signal at JasonMast.05. Wave Life Sciences’ experimental treatment for Duchenne muscular dystrophy hit the mark in a mid-stage study, setting the stage for a new ...
A local gas station, likely with a location near you, has successfully raised over $41,000 for the Muscular Dystrophy ...
Opens in a new tab or window Share on LinkedIn. Opens in a new tab or window A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...
Despite being known for more than 150 years, Duchenne muscular dystrophy (DMD) remains an untreatable disease affecting approximately 1 of every 3,500-5,000 males. Muscles in patients express no or ...
About Duchenne Muscular Dystrophy DMD is a progressive neuromuscular disorder caused by a mutation in the DMD gene which affects the production of a protein called dystrophin. 3 Dystrophin is a ...