Also read: India’s fight against rare diseases Rare diseases, particularly chronic genetic disorders, impose life-threatening challenges, often affecting children disproportionately. Alarmingly ...

Diagnosed with Ewing sarcoma at 9, Lucy Spada beat the odds and survived. Her family started the Little Warrior Foundation to ...

PHILADELPHIA, Feb. 6, 2025 /PRNewswire/ -- This year marks a monumental milestone for NephCure: 25 years of driving hope, innovation, and progress in the fight against rare kidney disease (RKD).

DMD is a rare ... heart disease, highlighting a critical unmet medical need. A previous study conducted at Vanderbilt University Medical Center demonstrated that ifetroban is protective against ...

Scientists have uncovered a mechanism for reinvigorating the immune system to stop it from flagging when it’s fighting ...

CPIX), a specialty pharmaceutical company with development efforts focused on new products for rare diseases, today announced positive top-line results from its Phase 2 FIGHT DMD trial.

PHILADELPHIA, Feb. 6, 2025 /PRNewswire/ -- This year marks a monumental milestone for NephCure: 25 years of driving hope, innovation, and progress in the fight against rare kidney disease (RKD).

PHILADELPHIA, Feb. 6, 2025 /PRNewswire/ -- This year marks a monumental milestone for NephCure: 25 years of driving hope, innovation, and progress in the fight against rare kidney disease (RKD).

KYIV, Ukraine (AP) — Ukraine wants to collaborate with partner countries on postwar projects worth billions of dollars not just in mining rare earth elements, but also in energy and construction ...

Lt. Col. Dr Aradhana Dwivedi, a Medical Geneticist with Army Hospital, said that although genetic/rare diseases are said to be 1 in 1000 children, in India the number is high due to the large ...

Set to enter hospice care, a patient with idiopathic multicentric Castleman's disease is now in remission after treatment with a medication identified by an AI-guided analysis.