Key to that mission is the “STEER” study, a late-stage trial of children with moderate SMA who are older than two years and have never before received certain targeted medicines like Zolgensma, Biogen ...

A pair of clinical data sets gives Novartis confidence in a new formulation of the company’s gene therapy Zolgensma for the treatment of older patients with spinal muscular atrophy (SMA).

The STEER study showed significant motor function improvement in children with SMA using intrathecal onasemnogene abeparvovec. The primary efficacy endpoint was met with a 2.39-point improvement ...

The pivotal trial enrolled only babies under 6 months. Two-year-olds born with the most common and severe form of SMA would likely have lost too many neurons to benefit from the therapy.

OAV101 IT, a version of the gene therapy Zolgensma (onasemnogene abeparvovec-xioi) that’s administered into the spinal canal, can be safely given to people with spinal muscular atrophy (SMA) who were ...

Although USB-C adapters are becoming more commonplace, you may still have old devices and chargers with USB-A ports. Rather than completely replacing them, buying a USB-C adapter sometimes makes more ...

Newly approved SMA therapies show promise but face global accessibility challenges, widening healthcare disparities due to high costs and limited availability. Newborn screening for SMA is ...

State Key Laboratory of Vaccines for Infectious Diseases, Center for Molecular Imaging and Translational Medicine, Xiang An Biomedicine Laboratory, School of Public Health, Xiamen University, 4221-116 ...

A woman is dead after a crash involving an SUV and a tractor in Clinton County Monday.It happened around 8:56 a.m. when troopers with the Ohio State Highway Patrol responded to a two-vehicle fatal ...

Private legal practitioner Martin Kpebu has weighed in on the ongoing legal battle between former Finance Minister Ken Ofori-Atta and the Office of the Special Prosecutor (OSP). The embattled former ...

The Office of the Special Prosecutor (OSP) has issued a stern warning to former Finance Minister Ken Ofori-Atta, stating that he will be re-listed as a wanted person should he fail to appear for ...