Pfizer shelves haemophilia gene therapy Beqvez

An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood ...
Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...
Revolutionary gene therapy approaches show promise in treating various retinal conditions, potentially transforming treatment ...
Bluebird Bio will sell itself to private equity firms Carlyle and SK Capital for about $30 million, the company said Friday.
Sensorion's Audiogene Phase I/II trial of the SENS-501 gene therapy programme has received a favourable recommendation from ...
A Connecticut boy is among four children all born with severe childhood blindness who gained “life-changing improvements” to ...
Eleven children who were legally blind at birth all gained visual acuity after receiving MeiraGTx's investigational gene ...
Latus Bio, Inc. (Latus), a biotechnology company pioneering advances in AAV gene therapy, is pleased to announce data ...
A groundbreaking gene therapy has restored sight in four young children born with severe blindness due to a rare genetic ...
Miltenyi Biotec launched India's first Cell and Gene Therapy Center in Hyderabad. The Miltenyi Innovation and Technology ...
At the Envision Summit 2025 in San Juan, Puerto Rico, Mike Farkas, MD, discussed gene therapy research for retinal ...